Due to extremely limited mobility, columnist Robin Stemple has already fallen twice in recent weeks. The next time could be ...

The Committee for Medicinal Products for Human Use (CHMP) has recommended that approval of Agamree (vamorolone) in the ...

The Speak Foundation launched the LGMD Centers of Excellence, a network of clinics dedicated to improving care for people ...

Wheelchairs tend to be equated with disability, but columnist Patrick Moeschen sees them as tools that increase function and ...

Muscular dystrophy refers to a group of genetic diseases that cause progressive muscle weakness and loss. There are more than 30 types of muscular dystrophy, all with different causes and symptoms.

Living with Duchenne muscular dystrophy (DMD) has affected my ability to do many things I used to love, such as brushing my teeth, dressing, sketching cartoons, eating snacks, handwriting assignments ...

“Take him home and give him a good life.” This was the main advice given to Jessica and Chris Curran by a genetic counselor after their son, Conner, was diagnosed with Duchenne muscular dystrophy (DMD ...

For parents and caregivers, a new diagnosis of Duchenne muscular dystrophy (DMD) can feel overwhelming. There’s no road map to managing the physical and mental changes in your child’s health, ...

Recognizing the early signs of Duchenne muscular dystrophy (DMD) may help slow its progression and alleviate DMD symptoms. DMD is a genetic condition that causes progressive muscle weakness and muscle ...

Betty Vertin is a mother and writer living in rural Hastings, Nebraska, with her husband and seven children. Betty is a caregiver to three sons, Max, Rowen, and Charlie. Her oldest was diagnosed with ...

Histone deacetylase inhibitors are a treatment approach designed to work by blocking an enzyme that turns off gene activity. This may ultimately help by slowing muscle loss and disease progression.

The investigational therapy DYNE-101 worked as expected and led to functional improvements for people with myotonic dystrophy type 1 (DM1) in a clinical trial, according to an update from developer ...