SKY-0515 takes an interesting approach to treating HD. Rather than targeting just one aspect of the disease, it reduces levels of two proteins involved in HD biology. The first is expanded huntingtin, ...
October was another busy month in Huntington’s disease (HD) research! We learned more about often-overlooked symptoms, ...
The FDA has accepted uniQure’s application for AMT-130 (now called ifezuntirgene inilparvovec), an experimental gene therapy ...
In plain language. Written by scientists. For the global HD community.