New one-dose treatment edits a gene in the liver, disabling the ANGPTL3 protein and significantly lowers cholesterol.

Molecular biologist Cynthia Kenyon speaks about her seminal discovery and excitement for the future of longevity research ...

Schizophrenia has long been one of medicine’s most puzzling conditions, with genetics offering tantalizing clues but an ...

Sickle cell disease is caused by a single genetic mutation that alters the shape of red blood cells. While the condition causes severe pain and health complications, carriers gain resistance to ...

A Northern Kentucky family is in a desperate search for answers as their 10-year-old boy battles a rare brain disorder.

A new study led by MUSC Hollings Cancer Center researchers Aaron Hobbs, Ph.D., and Rachel Burge, Ph.D., sheds light on why ...

A new study led by Aaron Hobbs, Ph.D., and Rachel Burge, Ph.D., at MUSC Hollings Cancer Center, reveals why a specific gene ...

Understanding human gene function in living organisms has long been hampered by fundamental differences between species.

A new single-cell profiling technique has mapped pre-malignant gene mutations and their effects in solid tissues for the ...

Maze Therapeutics uses its Compass genetics platform to advance kidney and obesity drugs, with MZE829 Phase 2 data due in ...

Genetic variants believed to cause blindness in nearly everyone who carries them actually lead to vision loss less than 30% ...