Whether a patient has ocular, limb/axial, or bulbar/respiratory MG may predict relapse risk after thymoma resection better ...

A retrospective study showed that autoantibody status in PBC was associated with specific hematologic and liver synthetic ...

An analysis of about 1.5 million individuals showed that genetic variants influencing IL12 signaling were associated with the ...

GV101, a ROCK2 inhibitor for Friedreich ataxia (FA) that may increase frataxin, received Fast Track designation from the FDA.

The L-index may help distinguish pseudohypertriglyceridemia caused by glycerol kinase deficiency from severe ...

Up to 75% of all OB/GYNs experience professional burnout, driven by a complex combination of clinical trauma, legal anxiety, ...

A mom shares why revaccinating her son, who has ALGS, brings up fears and how she works with their care team to overcome her ...

A new clinical development program, PALM, is testing TPIP in 3 active clinical trials in patients with PPF and other conditions.

The FDA placed a partial hold on Bright Minds’ planned trial of BMB-101, a 5-HT2C agonist for seizures linked to DEEs, including DS and LGS.

Leukoreduction may minimize transfusion-transmitted CMV risk in preterm infants, mitigating complications in FNAIT.

The median age at onset of MuSK-positive MG rose by 11 years from the 1980s to 2013 to 2025 at a tertiary center in Italy.

Acoramidis significantly reduced the decline in heart failure-related health status and health-related quality of life in ...