Wheelchairs tend to be equated with disability, but columnist Patrick Moeschen sees them as tools that increase function and ...

Upsher-Smith launched Kymbee support websites offering guidance on treatment, access, and care for DMD patients, caregivers, ...

Share this page with email Share this page on Facebook Share this page on X Share this page on Reddit Print Preferred Source on Google Last Saturday, I attended “Les Misérables: The Arena Spectacular” ...

A human being since 1972, Patrick Moeschen recently retired after 28 years of teaching music at the middle school level in a public school setting. Diagnosed with Becker muscular dystrophy (MD) in ...

An industry collaborative was formed with the goal of improving the design of clinical trials testing new treatments for FSHD ...

Columnist Betty Vertin affirms that being diagnosed with a rare disease like Duchenne MD doesn't diminish the value of her sons’ lives.

The FDA has given Mesoblast the go-ahead to launch a clinical trial testing its cell therapy remestemcel-L-rknd in children ...

Share this page with email Share this page on Facebook Share this page on X Share this page on Reddit Print Preferred Source on Google As I grow older with limb-girdle muscular dystrophy, one of my ...

Histone deacetylase inhibitors are a treatment approach designed to work by blocking an enzyme that turns off gene activity. This may ultimately help by slowing muscle loss and disease progression.

While Duchenne muscular dystrophy (DMD) is one of the most common types of this group of muscle-wasting disorders, affecting about 1 in 3,500 male births, each patient’s journey with this form of ...

Exon skipping is a treatment approach for people whose Duchenne muscular dystrophy is due to certain mutations in its causative gene. Exon skipping works like a molecular patch, so that the DMD gene ...