The US Food and Drug Administration has given the green light for the first gene therapy that treats a rare form of muscular dystrophy to be used in most people who have the disease and a certain ...
Solid Biosciences Inc. (Nasdaq: SLDB) (the “Company” or “Solid”), a life sciences company developing precision genetic ...
Scientists have developed a novel approach of genome editing to repair muscle stem (satellite) cells, offering new hope for ...
—Older age, presence of scoliosis, and other factors were associated with lower predicted forced vital capacity in patients with Duchenne muscular dystrophy using non-invasive ventilation. Individuals ...
A Community Event for Duchenne Muscular Dystrophy Awareness Brick, United States – January 1, 2026 / Steps for Hope 5K / The ...
Editor’s note: This is an automatically generated transcript. Please notify [email protected] if there are concerns regarding accuracy of the transcription. Muscular dystrophy, as a category, is quite ...
When Elie and Nancy Eid founded Save Our Sons Duchenne Foundation in 2008 after their first-born son Emilio was diagnosed with Duchenne muscular dystrophy, they could never have imagined how ...
Scientists are testing nearly two dozen treatments that might stop the disease. But enrollment in the trials is very restricted, and few children qualify. By Gina Kolata Lucas was 5 before his parents ...
Genethon is uniquely positioned to deliver long-term value and strategic collaboration opportunities in gene therapy.
CHARLESTOWN, Mass., Jan. 05, 2026 (GLOBE NEWSWIRE) -- Solid Biosciences Inc. (Nasdaq: SLDB) (the “Company”), a life sciences company developing precision genetic medicines for neuromuscular and ...
Darius Weems was diagnosed when he was just 5 years old. Nov. 22, 2012— -- Darius Weems is on a mission, but even though he is only 23 years old, it's a race against time. Darius, an aspiring ...
Duchenne muscular dystrophy (DMD) is the most common muscle disease in children and is passed on by X-linked recessive inheritance. Characteristic is a progressive muscular atrophy. Researchers have ...
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